Symposium on Translational Medicine and Biomanufacturing

• Clive Svendsen, PhD, Chair, California ALS Research Network, Cedars-Sinai Medical Center
• Dhruv Sareen, PhD, Executive Director, CS Biomanufacturing Center

• Keynote Lecture 1: Carl June, MD – University of Pennsylvania
  "CAR-T cells: Electing the Next Generation"

Note from our sponsor: Miltenyi

• Elizabeth Shpall, MD – University of Texas MD Anderson Cancer Center
  "CAR Therapy: Current Status and Future Directions"
• TJ Langer – Myst Therapeutics
  "Neoantigen enriched tumor-infiltrating lymphocyte (TIL) cell therapies"

Presentation by Kataoka

Theme II: Targeting Organ-Specific Diseases

• Eduardo Marban, MD, PhD – Cedars-Sinai 
  "Manufacturing therapeutic exosomes from progenitor cells"
• Arnold Caplan, PhD – Case Western Reserve University
  "MSCs and COVID-19"
• Katherine High, PhD – Rockefeller University
  "Turning genes into medicines: AAV-mediated gene transfer for genetic disease"

Lunch Break

Theme III: Brain and Eye Diseases

• Keynote Lecture 2: Sally Temple, PhD – Neural Stem Cell Institute
  "Advancing manufacture of an adult RPE stem cell therapy for age-related macular degeneration"

• Kapil Bharti, PhD National Eye Institute | National Institute of Health
  "Autologous iPS Cell-Based Therapy for Macular Degeneration: from Bench-to-Bedside"
• Clive Svendsen, PhD – Cedars-Sinai
  "A Phase 2a safety trial shows that engineered human neural progenitors survive and release GDNF in the spinal cord of ALS patients"

Presentation by Stemcell Technologies

Keynote Lecture 3

• David DiGiusto, PhD – Semma Therapeutics
  "Cell and Gene Therapy: Developing a Portfolio of Living Medicine"

Note from our sponsor: Biomerieux

• Derek Hei, PhD – Blue Rock Ventures
  "Addressing CMC Bottlenecks for iPSC Therapies"
• Dhruv Sareen, PhD – Cedars-Sinai
  "Manufacturing iPSCs and derivatives with cGMP"

Closing remarks and Thank you